Shares of drugmaker Sarepta Therapeutics surged in afterhours trading Monday after the company said it would resume shipping ...

2025 FEB 06-- By a News Reporter-Staff News Editor at Gene Therapy Daily News-- Researchers detail new data in Biotechnology- Gene Therapy. According to news reporting originating in Boston ...

This year, headlines in the cell and gene therapy landscape have so far been dominated by Sarepta. The biotech’s Duchenne muscular dystrophy treatment Elevidys (delandistrogene moxeparvovec) became ...

For the first time, we are witnessing therapies that can fundamentally alter the course of inherited disease lifelong. The most recent breakthrough describes treating inherited disease in infants ...

Sarepta is facing a number of issues currently, including platform-level safety concerns, management credibility issues, etc.

Kriya is advancing a host of gene therapies for a wide variety of chronic diseases, including geographic atrophy, trigeminal ...

Besides addressing lingering safety concerns, gene therapy is exploring applications beyond the correction of single-gene mutations. Possibilities include polygenic and gene-independent approaches.

Gene therapy holds promise to treat hereditary hearing loss, but while there has been progress, challenges remain, according to the authors of a recent review published in Sensory Neuroscience. 1 ...

Gene therapy is likely something you’ve seen or read about in the news, the most recent being how we can treat an enzyme deficiency with mRNA.

Gene therapy has been headline news in recent years, in part due to the rapid development of biotechnology that enables doctors to administer such treatments.